CGTLive

The FDA has announced it will be investigating reports of hematologic malignancies—namely cases of myelodysplastic syndrome and acute myeloid leukemia—in patients with #CALD who were treated with bluebird bio's elivaldogene autotemcel (#Skysona).

ICYMI: In the patients treated at the high dose in the trial, 15% to 85% (mean, 54%) of muscle fibers showed expression of microdystrophin at 8 weeks posttreatment. #genetherapy #MuscularDystrophy #Duchenne Genethon Read more: https://lnkd.in/eujge_dG

Tenaya Therapeutics anticipates reporting initial data from the trial next year. #cardiomyopathy #cardiology #genetherapy Read more: https://lnkd.in/eJN3pN3V

In honor of #AlzheimersDiseaseAwarenessMonth, observed annually in November, CGTLive® took a look back at some of the progress that has been made for cell therapy and gene therapy candidates in #Alzheimers over the past year. #AlzheimersDisease More: https://lnkd.in/e65guk9H

The FDA has approved StemCyte Inc.’s Regenecyte for use in unrelated donor hematopoietic progenitor cell transplantation procedures alongside an appropriate preparative regimen. #celltherapy #CordBlood #StemCells Read more: https://lnkd.in/eSckWAtT

ICYMI: •Atamyo Therapeutics's Gene Therapy ATA-200 Cleared for US Trial in #LGMD Type 2C/R5 •First Patient Dosed in Trial for Adicet Bio, Inc's T-Cell Therapy ADI-100 in #AutoimmuneDisease Review more top news and interview highlights in #celltherapy and #genetherapy from the week ending Nov 22, 2024: https://lnkd.in/g-s37TPz

In the patients treated at the high dose in the trial, 15% to 85% (mean, 54%) of muscle fibers showed expression of microdystrophin at 8 weeks posttreatment. #genetherapy #MuscularDystrophy #Duchenne Genethon Read more: https://lnkd.in/eujge_dG

•Atamyo Therapeutics's Gene Therapy ATA-200 Cleared for US Trial in #LGMD Type 2C/R5 •First Patient Dosed in Trial for Adicet Bio, Inc's T-Cell Therapy ADI-100 in #AutoimmuneDisease Review more top news and interview highlights in #celltherapy and #genetherapy from the week ending Nov 22, 2024: https://lnkd.in/g-s37TPz

ICYMI: In honor of #WorldPancreaticCancerDay, held on the third Thursday of November each year, CGTLive® took a look back at progress for #celltherapy and #genetherapy candidates in #PancreaticCancer over the past year. #PancreaticCancerAwareness More: https://lnkd.in/eFQHqPpG

ICYMI: • CSL Behring Shuttering #Pasadena Facility • Anixa Biosciences, Inc. Moves Onto Third Cohort in Trial for #OvarianCancer CER-T Have a #celltherapy or #genetherapy update you’d like to share? Tag us with #AroundTheHelix! https://lnkd.in/eFEK57Sg