Ammar Sabir Cheema, PhD’s Post

Unlocking gene regulation with sequence-to-function models https://lnkd.in/dUm3wRAZ

What drives the work that Travis Hardcastle does to move cell and gene therapy innovation forward? It's a desire to make an impact on people's lives, and to potentially find cures for challenging genetic diseases. Learn more about how Travis and researchers across the world are using #OGM to assess genome integrity and transform cell and gene therapy programs: https://bit.ly/4blDOJ4 #CGT #cellandgenetherapy #genomeintegrity #Bionano

Treating and/or curing genetic-based rare and orphan diseases is a lofty task. But cell and gene therapy has unprecedented potential. Find out what three characteristics can support a successful #nonclinical program: https://bit.ly/4dW8UZ8 #CGT #CellTherapy #GeneTherapy #NonclinicalPrograms #RareDiseases

On RNA Day, CoJourney spotlights the vital role RNA plays in gene therapy and the groundbreaking research at CoJourney. RNA isn’t just a molecule—it’s a key to unlocking new treatments and advancing personalized medicine. Today, we celebrate the science that propels us forward and the potential RNA holds for transforming lives. Here’s to the future of genetic innovation! #RNADay #GeneTherapy #ScientificBreakthroughs #PersonalizedMedicine #HealthInnovation #RNA #GeneticAdvancements #GeneticResearch #FutureOfMedicine #CoJourney

Gene therapies are key to advancing innovative treatments for conditions with unmet needs. Dr. Marks and Dr. Miller discuss the various types of gene therapy currently in play and where AI could be at it’s best in this space in this episode of Science With a Twist.

Gene therapies are key to advancing innovative treatments for conditions with unmet needs. Dr. Marks and Dr. Miller discuss the various types of gene therapy currently in play and where AI could be at its best in this space in this episode of Science With a Twist.

Ever wondered about the powerhouse driving gene-editing breakthroughs? It's CRISPR-Cas9, a revolutionary technology that's transforming medicine. 🧬 CRISPR-Cas9 acts like molecular scissors, precisely snipping DNA to correct genetic defects or insert beneficial genes. This paves the way for potential cures to a myriad of genetic disorders. The recent study published in Scientific Reports demonstrates a leap in gene therapy using CRISPR-Cas9 and CRISPR-Cas12a, enabling safer and more precise in vivo gene targeting. Read here:https://lnkd.in/gt7CzZAS #Tsingke #TsingkeInsights #GeneEditing #CRISPRCas9

Explore how NCATS scientists used #GeneEditing and 3-D human cell models to study the genetics of polycystic #KidneyDisease (PKD), a life-threatening inherited kidney disorder. This new platform allows us to further study the genetics of #PKD and discover possible treatments for the millions of people affected by it. Read about how researchers are using gene editing to correct gene mutations: https://go.nih.gov/f7kDTet

Gene therapies are key to advancing innovative treatments for conditions with unmet needs. Dr. Marks and Dr. Miller discuss the various types of gene therapy currently in play and where AI could be at its best in this space in this episode of Science With a Twist.

Looking for some summer learning? Check out Thermo Fisher's Basic Gene Therapy Education Series! Gene therapy provides a promising way to treat inherited and acquired diseases via transfer of genetic material. In this knowledge culture basic education series on lentiviral vectors, delve into principles of lentiviral transduction and challenges in suspension-based lentivirus production as well as lentiviral vector purification and associated analytics.