May 2023 News from CRD
Cure Rare Disease
501(c)(3) nonprofit leading a nationwide collaboration of researchers and clinicians to develop customized therapeutics.
To Our Community:
This month, we published a case report with the comprehensive findings from the CRD-TMH-001 clinical trial. We have made this manuscript available via an open access server as part of our commitment to sharing information that may benefit the rare disease community, while we concurrently submit our manuscript to a peer-review journal.
In addition to the full report published on medRXiv.org, we encourage our community to visit the FAQ section on our website, where we address common questions related to the trial, steps the organization is taking based on what was learned from the study, and more.
CRL Presented the Terry Horgan Pioneer Award
During the CRL 6th World Congress, Charles River presented the "Terry Horgan Pioneer Award" to Emily Whitehead in Terry’s honor. Emily was the first pediatric CAR T patient and is now 11 years cancer-free.
"We honor him today because we can also call him courageous, inspirational and a true medical pioneer, who put his faith in his family, the science and his medical team to participate in a clinical trial for the first in human CRISPR therapy for DMD. This was not blind faith, Terry was an integral part of his drug development which was lead by his brother, Rich Horgan,” said Barbara Killian, Associate Director Discovery, Charles River.
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Run in the Disneyland Half Marathon Weekend
We are thrilled to share that CRD will be part of the runDisney Disneyland Half Marathon Weekend on January 11-14, 2024 in Disneyland CA.
Join our team before spots sell out and don't miss your chance to experience the magic of the happiest place on earth while running for a great cause!
Bryan Boys for Hope Zippy Mile Raises over $23,000 for CRD
The Bryan Family raised $23,640 for the Bryan Boys for Hope Zippy Mile as part of the Sioux Falls Half Marathon in Sioux Falls, SD!
Thank you to all who participated and to the Bryan Family! Read more about their event and see photos in our latest blog.
Have an idea for a fundraiser or want to participate in an endurance race in your area? Email Danielle Garrigan to get started.