ITF Therapeutics LLC

𝘌𝘯𝘨𝘶𝘭𝘧𝘦𝘥 𝘪𝘯 𝘊𝘢𝘳𝘦𝘨𝘪𝘷𝘪𝘯𝘨: 𝘈 𝘗𝘰𝘳𝘵𝘳𝘢𝘪𝘵 𝘰𝘧 𝘓𝘰𝘷𝘦, 𝘌𝘯𝘥𝘶𝘳𝘢𝘯𝘤𝘦, 𝘢𝘯𝘥 𝘜𝘯𝘳𝘦𝘭𝘦𝘯𝘵𝘪𝘯𝘨 𝘕𝘦𝘦𝘥 is a must-read for anyone trying to understand what it’s like to support a loved one with Duchenne muscular dystrophy (DMD). We have shared a copy with everyone on the ITF team. Three caregivers whose stories are presented in this enlightening resource - Bill Barton, Mary Garrison, and Vivian McSween - recently shared their stories with us. We were humbled to learn how they cope with intense physical, emotional, financial, and logistical challenges while still finding moments of joy and resilience. Thank you to our co-host Marissa Penrod, Founder of Team Joseph, and to all our guest speakers for taking the time to connect with us, answer questions, and share your stories. We are grateful for the opportunity to learn from you. The personal experiences and insights you shared will continue to have an incredible impact on the work we do each and every day. #Duchenne #DMD #RareDiseases

Thank you to CureDuchenne for hosting an engaging Caregiver Dinner Session in Portland, OR. We appreciated this opportunity to listen and learn from stories shared by members of the neuromuscular disease community, including individuals living with Duchenne muscular dystrophy and their families.   To learn more about upcoming #CureDuchenneCares Caregiver Dinner Sessions, visit: https://lnkd.in/gpF-RgQk   #Duchenne #DMD #RareDiseases

Thank you to the American Academy of Physical Medicine & Rehabilitation (AAPM&R) for hosting an outstanding #AAPMR24 Annual Assembly in San Diego, CA. We enjoyed engaging with researchers and clinicians across the physical medicine and rehabilitation space to discuss new developments that are shaping the future of care for people living with neuromuscular diseases, including Duchenne muscular dystrophy (DMD). We were also excited to join the medical community in congratulating Craig McDonald, M.D., FAAPMR, of UC Davis Health on receiving the AAPM&R Distinguished Member Award! This important recognition honors the critical role that Dr. McDonald has played in advancing neuromuscular medicine, and we are especially grateful for his significant contributions to research in DMD. #Duchenne #DMD #RareDiseases

We were honored to attend and support the “Investing in Every Future” event held in New York, NY, to celebrate the important milestones that Parent Project Muscular Dystrophy (PPMD) has achieved over the past 30 years. For three decades, PPMD has played a central role in accelerating research, shaping policy, and advancing care for people living with Duchenne muscular dystrophy (DMD) and their families. As we reflect on the impressive progress that was commemorated throughout the event, we find ourselves even more excited about the work that lies ahead to help build a brighter future together. During our time in New York, we also participated in the PPMD Duchenne Drug Development Roundtable focused on identifying opportunities to support the unique needs and goals of the DMD community. We are grateful to be part of these critical conversations and to collaborate with dedicated advocates and organizations working to drive meaningful change for people living with DMD and their families. #Duchenne #DMD #RareDiseases

As Tucker started to experience more mobility challenges associated with Duchenne muscular dystrophy (DMD), his parents Jordan and Jamie Howe recognized that their home was no longer safe or accessible for him. The solution? Building a new, accessible home by hand with the support of their close relatives. Read more about the Howe family’s experience with DMD in this Patch.com article: https://lnkd.in/eTbf56_v #Duchenne #DMD #RareDiseases

We were honored to join the neuromuscular disease community at the Muscular Dystrophy Association Engage Symposium held in Stanford, CA. Throughout the event, we had the chance to connect with and learn from attendees including individuals living with Duchenne muscular dystrophy and their families, in addition to hearing updates on the latest advancements in research and care.   For more information about future MDA Engage events, visit: https://lnkd.in/dMpBr82E   #Duchenne #DMD #RareDiseases

Our team was pleased to attend the University of Utah Program for Inherited Neuromuscular Disorders Family Conference held in Draper, UT. This important event brought together leading researchers, clinicians, and families for insightful discussions about the role of collaboration in supporting the advancement of research in neuromuscular diseases, including Duchenne muscular dystrophy. Learn more about the Utah Program for Inherited Neuromuscular Disorders here: https://lnkd.in/e3j7MQVa #Duchenne #DMD #RareDiseases

On #LGBTQStemDay, we are proud to honor LGBTQIA+ professionals in STEM fields whose contributions have played a critical role in advancing research in life sciences, including supporting the discovery and development of solutions for rare disease communities. We believe that fostering inclusive environments where diverse perspectives are celebrated is crucial to help drive progress in science and healthcare.   To learn more about activities planned for LGBTQ+ STEM Day from Pride in STEM visit: https://lnkd.in/gArFzhh

Italfarmaco is proud to sponsor an ISPOR Educational Webinar on December 4th 2024, titled: “Leveraging the Value of Clinical Outcomes in DMD for Decision Making”. The webinar will be moderated by Dr. Francois Meyer and will include talks from three highly distinguished experts in DMD: Prof. Valeria Sansone; Conny Pelicaen and Dr. Paolo Bettica. Don’t miss the opportunity to gain insights into DMD, from understanding disease progression to navigating key disease milestones, as well as the complexities of clinical trial design in this therapeutic area. Discover the importance of collaboration among patient advocates, clinicians, and industry to improve patient access to innovative treatments. Italfarmaco’s rare diseases mission is to bring new opportunities to the rare diseases community, with innovation, quality, knowledge and motivation that can help more people su­ffering from rare diseases, than ever before. For additional information: https://lnkd.in/epmWhwBm

Our marketing team strives to support shared decision making among doctors, patients, and caregivers. Read more about this approach in our latest blog post by Dan O'Connell, VP, Head of US Marketing: https://lnkd.in/eteMds3x #Duchenne #DMD #RareDiseases